Molecular systems for improving gene mutation correction in muscle disease

Authors

Robert M. Kapsa, University of WollongongFollow
Gilles Gasser, University of ZurichFollow
Joselito M. Razal, University of WollongongFollow
Anita Quigley, University of WollongongFollow
Tanmaya Joshi, Monash University
Simon Moulton, University of WollongongFollow
Mark J. Cook, University of Wollongong
Leone Spiccia, Monash University
David Officer, University of WollongongFollow
Graeme M. Clark, Latrobe University
Gordon G. Wallace, University of WollongongFollow

RIS ID

45870

Publication Details

Kapsa, R. M., Gasser, G., Razal, J., Quigley, A., Joshi, T., Moulton, S., Cook, M. J., Spiccia, L., Officer, D., Clark, G. M. & Wallace, G. G. (2011). Molecular systems for improving gene mutation correction in muscle disease. Journal of Gene Medicine, 13 (7-8), 437-438.

Abstract

Targeted corrective gene conversion (TCGC) holds much promise as a future therapy for many hereditary diseases in humans, but there still remain significant impediments to effective mutation correction and it is clear that significant work remains to improve TCGC to levels where it can be considered for translation to the clinical setting.

Grant Number

ARC/FF0669110, ARC/DP0987503

Additional Grant Number

http://purl.org/au-research/grants/ARC/FF0669110

http://purl.org/au-research/grants/ARC/DP0987503